Diagnosgrupp
NT-rådets rekommendationer sorterade efter sjukdom.
Tumörsjukdomar
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- Axikabtagen ciloleucel (Yescarta)
- Belantamab mafodotin (Blenrep)
- Blinatumomab (Blincyto)
- Brexukabtagen autoleucel (Tecartus)
- Ciltakabtagen-autoleucel (Carvykti )
- Daratumumab (Darzalex)
- Elotuzumab (Empliciti)
- Genmodifierade autologa stamceller (Zynteglo)
- Idekabtagen-vikleucel (Abecma)
- Inotuzumab ozogamicin (Besponsa)
- Isatuximab (Sarclisa)
- Ixazomib (Ninlaro)
- Karfilzomib (Kyprolis)
- Lisokabtagen-maraleucel (Breyanzi)
- Mosunetuzumab (Lunsumio)
- Obinutuzumab (Gazyvaro)
- Polatuzumab vedotin (Polivy)
- Tafasitamab (Minjuvi)
- Tisagenlekleucel (Kymriah)
Övriga diagnosgrupper
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- Anifrolumab (Saphnelo)
- Ataluren (Translarna)
- Atidarsagen-autotemcel (Libmeldy)
- Avalglukosidas alfa (Nexviadyme)
- Burosumab (Crysvita)
- Dextrometorfan/kinidin (Nuedexta)
- Eculizumab (Soliris)
- Eladokagen-exuparvovek (Upstaza)
- Elexakaftor/tezakaftor/ivakaftor (Kaftrio)
- Elosulfas alfa (Vimizim)
- Inotersen (Tegsedi)
- Kaplacizumab (Cablivi)
- Krizanlizumab (Adakveo)
- Mogamulizumab (Poteligeo)
- Nusinersen (Spinraza)
- Olipudas alfa (Xenpozyme)
- Onasemnogen-abeparvovek (Zolgensma)
- Patisiran (Onpattro)
- Pegcetakoplan (Aspaveli)
- Ravulizumab (Ultomiris)
- Risdiplam (Evrysdi)
- Tafamidis (Vyndaqel)
- Tofersen (Qalsody)
- Valoktokogen-roxaparvovek (Roctavian)
- Vosoritid (Voxzogo)
- Vutrisiran (Amvuttra)